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Sarepta Therapeutics Inc. (formerly AVI Biopharma Inc., before that Antivirals Inc.) is developing applications of Morpholino oligos for therapeutics and is pursuing clinical trials with several Morpholinos. In their literature, Morpholino oligos are often referred to as PMOs or Neugenes.

The research program at Gene Tools to develop effective in vivo delivery technology for Morpholino oligos is intended to enhance the efficacy of Morpholino oligos for therapeutic applications as well as to simplify the use of Morpholinos in vivo for fundamental biological research and pharmaceutical target validation.