Authors: Cripe L, Colan S. Eliopoulos H, Moody S, Mendell JCitation: Neuromusc Disord. 2017;27(suppl 2):S114 doi:10.1016/j.nmd.2017.06.083Epub: Not EpubLink to Publication: http://www.nmd-journal.com/article/S0960-8966(17)30656-9/abstractOrganism or Cell Type: humanDelivery Method: i.v. infusion